[WCN23_Free Paper]
POSITIVE RESULTS FROM A FIRST-IN-HUMAN STUDY SUPPORTING CONTINUED DEVELOPMENT OF PGN-EDO51 FOR THE TREATMENT OF DUCHENNE MUSCULAR DYSTROPHY (DMD)
Michelle Mellion (United States of America)
A NEW PATIENT-REPORTED OUTCOME MEASURE FOR THE ASSESSMENT OF DYSPHAGIA IN OCULOPHARYNGEAL MUSCULAR DYSTROPHY: THE DYSPHAGIAMETER
Claudia Cote (Canada)
OUTCOME OF GUILLAIN-BARRÉ SYNDROME WITH BULBAR PALSY
Jayantee Kalita (India)
DESIGN OF A PHASE 2 CLINICAL PROGRAM FOR THE DEVELOPMENT OF PGN-EDO51 IN PARTICIPANTS WITH DUCHENNE MUSCULAR DYSTROPHY (DMD)
Michelle Mellion (United States of America)
PREDIABETES DISRUPTS LACTATE TRAFFICKING IN PERIPHERAL NERVES: A NOVEL MECHANISTIC TARGET?
Eva L. Feldman (United States of America)
18 Oct 2023