Created 2024-01-15 14:16 by an administrator; Last edited 2024-01-25 12:54 by an administrator

Neuropathies and Muscle Disease

[WCN23_Free Paper]

Neuropathies and Muscle Disease

POSITIVE RESULTS FROM A FIRST-IN-HUMAN STUDY SUPPORTING CONTINUED DEVELOPMENT OF PGN-EDO51 FOR THE TREATMENT OF DUCHENNE MUSCULAR DYSTROPHY (DMD) 
Michelle Mellion (United States of America)

A NEW PATIENT-REPORTED OUTCOME MEASURE FOR THE ASSESSMENT OF DYSPHAGIA IN OCULOPHARYNGEAL MUSCULAR DYSTROPHY: THE DYSPHAGIAMETER
Claudia Cote (Canada)

OUTCOME OF GUILLAIN-BARRÉ SYNDROME WITH BULBAR PALSY
Jayantee Kalita (India)

DESIGN OF A PHASE 2 CLINICAL PROGRAM FOR THE DEVELOPMENT OF PGN-EDO51 IN PARTICIPANTS WITH DUCHENNE MUSCULAR DYSTROPHY (DMD)
Michelle Mellion (United States of America)

PREDIABETES DISRUPTS LACTATE TRAFFICKING IN PERIPHERAL NERVES: A NOVEL MECHANISTIC TARGET?
Eva L. Feldman (United States of America)

18 Oct 2023